CSL Behring donates to WFH
500 Million IUs Coagulation Factor Replacement Therapy for the World Federation of Hemophilia Humanitarian Aid Program.
From then to now...
On Word Hemophilia Day we reaffirm our mission to create best-in-calss treatments for haemophilia
EMA starts Review of Gene Therapy
EMA Commences Review of Novel Gene Therapy Candidate Etranacogene Dezaparvovec for People with Hemophilia B
Historic University lights up on Rare Disease Day
Under the motto "Share Your Colors", we are setting an example for the 300 million people living with a rare disease.
A Book for Children with Rare Diseases
We chatted with mother-and-son team Evren and Kara Ayik, authors of a new book that’s for, and about, kids who have rare dise…
The UN Recognizes Rare Disease Patients
Supporters hope a newly adopted U.N. resolution will make rare disease patients more visible and ensure they have access to c…